Patent Leaderboard
USPTO Patent Rankings Data through Dec 31, 2025
Home › Compositions and methods for treating spinal muscular atrophy

Compositions and methods for treating spinal muscular atrophy

US Patent 10821154 · Granted Nov 3, 2020

Assignee

Inventors

View full patent text on Google Patents →

More Patents by These Inventors

Modulation of dystrophia myotonica-protein kinase (DMPK) expression2025
Enhanced delivery of viral particles to the striatum and cortex2025
Exon skipping oligomer conjugates for muscular dystrophy2025
Gene therapy for neurodegenerative disorders2025
Gene therapy for neurodegenerative disorders2025
Gene therapy for neurodegenerative disorders2025
Variant RNAi2025
Modulation of huntingtin expression2025
Modulation of huntingtin expression2025
AAV vectors for retinal and CNS gene therapy2025
Gene therapy for retinitis pigmentosa2025
Modified antisense oligomers for exon inclusion in spinal muscular atrophy2024